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Disease ReportsNiemann-pick diseases
MeSH D009542 - niemann-pick diseases
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Competitive Landscape
Events Timeline
Commercial
Clinical Trials
Competitive landscape
D013106:Sphingolipidoses
0 Companies
0 Drugs
Success rate
D015616:Non-langerhans-cell histiocytosis
0 Companies
0 Drugs
Success rate
D009542: 
Niemann-pick diseases
$
Success rate
D052536:Type a niemann-pick disease
0 Companies
0 Drugs
Success rate
D052537:Type b niemann-pick disease
0 Companies
0 Drugs
Success rate
D052556:Type c niemann-pick disease
0 Companies
0 Drugs
Success rate
Events Timeline
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Commercial
Company Name
Drug Name
Trade Name
Patent Expires
Approval Date
Revenue
Period
Johnson & JohnsonMiglustat Zavesca  2002-11-20   
Clinical Trials
Historical Success Rate
Phase 1
33%
1/3
Phase 2
67%
2/3
Phase 3
33%
1/3
Approved: 1Overall Success rate: 7%
All Clinical Trials
No data
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